Sickle Cell Disease Community

Together, We Can Improve Lives

SCD Community Resources

Clinical trials are an important step in finding new and improved ways to identify and treat diseases. In fact, all of the medications and treatments available to us today have been tested as part of a clinical research study or clinical trial. By participating in a clinical trial for sickle cell disease (SCD), you could help researchers learn more about disease and create new treatments that can improve the lives of people with SCD.

The ASH Research Collaborative™ Sickle Cell Disease Clinical Trials Network helps educate the SCD community about clinical trials. We’ve created a number of resources to help inform participants and their caregivers about why clinical trials are important, and how they can get involved.

Clinical Trials 101

Why Participate in Clinical Trials for Sickle Cell Disease

If you are new to clinical research or would like some additional information on clinical trials please download the
Why Participate in Clinical Trials for Sickle Cell Disease Brochure.

Gene Therapy for Sickle Cell Disease

Sickle cell disease occurs when a person inherits a faulty gene, which controls how red blood cells produce hemoglobin. Hemoglobin is the oxygen-carrying protein in red blood cells. Without enough healthy hemoglobin, red blood cells become stiff and sickled, which leads to inflammation and damage to blood vessels.

Gene Therapy for SCD

The Promise of Gene Therapy

Gene therapy and gene editing may offer a one-time treatment that addresses the genetic cause of sickle cell disease.