Latest News for: atrophy

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Stoke Therapeutics Announces First Patient Dosed in Phase 1 Study of STK-002, a Potential Disease-Modifying Medicine for the Treatment of Autosomal Dominant Optic Atrophy (ADOA)

Pharmiweb 11 Feb 2026
... patient has been dosed in the Phase 1 OSPREY study of STK-002, an investigational medicine for the treatment of Autosomal Dominant Optic Atrophy (ADOA) ... About Autosomal Dominant Optic Atrophy (ADOA).
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Fertility Authority Flags Genetic Threat in European Donor Sperm

Greek City Times 08 Feb 2026
... screening requirements for spinal muscular atrophy (SMA) in donor sperm.
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ZipBio and MeiraGTx Enter into Exclusive License Agreement to Advance First-in-Class AAV Gene Therapy for Geographic Atrophy

PR Newswire 03 Feb 2026
Under the agreement, MeiraGTx will receive exclusive rights to ZipBio's first-in-class therapies for Geographic Atrophy, targeting the complement pathway.
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Child’s right leg continually atrophies without diagnosis

Image Idaho Press-Tribune 29 Jan 2026
Six-year-old Valerie Jensen spent the summer riding bikes, playing on playgrounds and running with all the other kids her age ... .
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Medical Mystery: Child’s right leg continually atrophies without diagnosis

Image Idaho Press-Tribune 28 Jan 2026
Six-year-old Valerie Jensen spent the summer riding bikes, playing on playgrounds and running with all the other kids her age ... .
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Are you suffering from “cognitive atrophy” due to AI overuse?

PsyPost 23 Jan 2026
As an expert on how new technology reshapes society and the human experience, I have observed a growing phenomenon which I and other researchers refer to as “cognitive atrophy” ... Recognising atrophy.
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Children ‘robbed’ of better quality of life: Test delays affecting babies born with spinal muscular atrophy

The Irish Times 21 Jan 2026
At 12-weeks-old, Donnacha was diagnosed with spinal muscular atrophy (SMA) type 1, a rare genetic condition that increases his risk of severe respiratory illness due to muscle weakness ... atrophy.
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Ocugen Announces Positive Preliminary Phase 2 Data from OCU410 Modifier Gene Therapy for Geographic Atrophy ...

Nasdaq Globe Newswire 15 Jan 2026
... its novel modifier gene therapy for geographic atrophy (GA) secondary to dry age-related macular degeneration (dAMD).
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Ocugen Announces Positive Preliminary Phase 2 Data from OCU410 Modifier Gene Therapy for Geographic Atrophy Secondary to Dry Age-Related Macular Degeneration (Form 8-K) (Ocugen Inc)

Public Technologies 15 Jan 2026
for Geographic Atrophy Secondary to Dry Age-Related Macular Degeneration · Phase 2 (~50% of patients evaluated to date at 12 months) shows 46% lesion growth reduction vs ... About dAMD and Geographic Atrophy.
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Spinal Muscular Atrophy Pipeline 2025: FDA Approvals and Clinical Trials Landscape with MOA and ROA ...

GetNews 15 Jan 2026
The Spinal Muscular Atrophy Pipeline report embraces in-depth commercial and clinical assessment of the pipeline products from the pre-clinical developmental phase to the marketed phase ... Spinal Muscular Atrophy Overview.
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Biogen Receives European Commission Approval for High Dose Regimen of SPINRAZA� (nusinersen) for Spinal Muscular Atrophy

Nasdaq Globe Newswire 12 Jan 2026
... (EC) has granted marketing authorization for a high dose regimen of SPINRAZA� (nusinersen) which is comprised of 50 mg/5 mL and 28 mg/5 mL doses for the treatment of 5q spinal muscular atrophy (SMA).
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Biogen Receives European Commission Approval for High Dose Regimen of SPINRAZA® (nusinersen) for Spinal Muscular Atrophy (Biogen Inc)

Public Technologies 12 Jan 2026
BIIB) today announced the European Commission (EC) has granted marketing authorization for a high dose regimen of SPINRAZA® (nusinersen) which is comprised of 50 mg/5 mL and 28 mg/5 mL doses for the treatment of 5q spinal muscular atrophy (SMA).
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'I know Jesy Nelson's pain — because my child was born with spinal muscular atrophy'

The Mirror 09 Jan 2026
Little Mix singer Jesy Nelson took to Instagram and shared the heartbreaking news her twins, Ocean Jade and Story Monroe, had been diagnosed with spinal muscular atrophy (SMA) ... .
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As Jesy Nelson launches campaign for NHS to screen ALL newborns for spinal muscular atrophy ...

The Daily Mail 08 Jan 2026
The UK is a global outlier in relation to newborn SMA screening, which is currently in place within the United States and across most of Europe ....
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Complement Therapeutics Announces FDA Fast Track Designation for CTx001 for the Treatment of Geographic Atrophy Secondary to AMD

PR Newswire 08 Jan 2026
Food and Drug Administration (FDA) has granted Fast Track Designation for CTx001, the company's lead gene therapy candidate for the treatment of Geographic Atrophy (GA) secondary to Age-related Macular Degeneration (AMD).

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